Presented in a poster at the 2026 MDA Clinical & Scientific Conference, the approval is supported by data from the Phase 3 ADAPT SERON study, a randomized, double-blind, placebo-controlled trial ...

Entrada Therapeutics to Announce Topline Results from Cohort 1 of Participants with Duchenne Muscular Dystrophy Treated with ENTR-601-44 in Phase 1/2 ELEVATE-44-201 Study on May 7 ...

Epicrispr Biotechnologies (“Epicrispr”), a clinical-stage company pioneering gene-modulating therapies, and Forge Biologics (“Forge”), a leading manufacturer of gene therapies and member of the ...

The annual MDA Muscle Walk brings families and supporters together, raising funds, hope and awareness for muscular dystrophy ...

Jake Kirchner wanted to play baseball in Belle Plaine. This spring, he is, in a way. Mike Max explains.

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An AI-powered exoskeleton stole the spotlight at China’s Canton Fair after helping a patient with muscular dystrophy walk ...

During ALS Awareness Month this May, the Muscular Dystrophy Association (MDA) is highlighting unprecedented scientific progress, inspiring personal stories, legislative advocacy, and national ...

During ALS Awareness Month this May, the Muscular Dystrophy Association (MDA) is highlighting unprecedented scientific progress, inspiring personal stories, legislative advocacy, and ...

Santhera Pharmaceuticals (SIX: SANN) today announced that the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has adopted a positive opinion recommending ...

A gamer known for beating some of gaming's toughest challenges without the use of traditional controllers is beating Super ...

There were 11 awards presented, celebrating success in volunteering, fundraising, caring, campaigning, community support and research. Individuals were ...