Presented in a poster at the 2026 MDA Clinical & Scientific Conference, the approval is supported by data from the Phase 3 ADAPT SERON study, a randomized, double-blind, placebo-controlled trial ...

Twin brothers Daniel and Matt Murray of Buffalo are preparing to take on three marathons together to raise awareness and funds for Duchenne muscular dystrophy, a condition Matt has lived with his ...

The annual MDA Muscle Walk brings families and supporters together, raising funds, hope and awareness for muscular dystrophy ...

The children who receive pediatric therapy services often face some of their greatest challenges in the classroom. The ...

The global pharmaceutical industry is at a critical inflection point. While the FDA Modernization Act 2.0 has cleared the path for Non-Animal Models (NAMs), the transition from legacy animal testing ...

Imagine a world where you don’t have to wait for help to get out of bed, go to the bathroom, or reach for a favorite snack in ...

Steffni Randale, a Lubbock native living with the rare Duchenne Muscular Dystrophy, is featured in TLC’s new show “One Day in ...

Get the latest news about Leah Messer. Find exclusive interviews, video clips, photos and more on Entertainment Tonight.

Entrada Therapeutics to Announce Topline Results from Cohort 1 of Participants with Duchenne Muscular Dystrophy Treated with ENTR-601-44 in Phase 1/2 ELEVATE-44-201 Study on May 7 ...

Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare ...

Ms. Rosenberg didn’t know it at the time, but she had both obsessive-compulsive disorder and body dysmorphic disorder, or B.D ...

The decision lifts Louisiana’s need to have two majority-Black districts. But Gov. Jeff Landry (R) seems intent on maximizing his party’s gain from the decision, potentially with a map that picks up ...